A leader in human being gene therapy.

AMT enters contract with Consortium for clinical development of novel gene therapy to take care of Sanfilippo B Amsterdam Molecular Therapeutics , a leader in human being gene therapy, announced today that it has entered into an contract with Institut Pasteur, Paris, France, and several French analysis institutes to support clinical development of a novel gene therapy to treat Sanfilippo B suhagra . This rare genetic disease affecting new-born children leads to progressive neuronal degeneration and death. There is no approved therapy available.